Ionis reports positive zilganersen data for Alexander disease

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Ionis presents new data from pivotal study of zilganersen in Alexander disease (AxD) at AAN 2026 Annual Meeting

April 21, 2026 7:00 AM EDT

New data highlight potential treatment benefit across multiple AxD symptom domains, reinforcing zilganersens positive impact on people living with this rare, often fatal neurological disease

PDUFA date set for September 22, 2026

CARLSBAD, Calif.--(BUSINESS WIRE)-- Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) today announced additional positive results from the pivotal... More