PTC Therapeutics receives FDA approval for PKU treatment drug

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PTC Therapeutics Announces FDA Approval of Sephience™ (sepiapterin) for the Treatment of Children and Adults Living with Phenylketonuria (PKU)

July 28, 2025 4:19 PM EDT

- Broad labeling inclusive of all disease subtypes for individuals 1 month of age and older -

- PTC will host a conference call on Monday, July 28th at 5:00 pm ET -

WARREN, N.J., July 28, 2025 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) announced today that the... More