Agios Pharma (AGIO) Reports Results from Phase 3 ACTIVATE-KidsT Study of Mitapivat

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Agios Announces Results from Phase 3 ACTIVATE-KidsT Study of Mitapivat in Children with PK Deficiency Who Are Regularly Transfused

August 1, 2024 6:30 AM EDT

ACTIVATE-KidsT is Agios First Pediatric Data Readout;
Safety Results Consistent with Safety Profile for Mitapivat Previously Observed in Adults
with PK Deficiency Who are Regularly Transfused

Prespecified Statistical Criterion for the Primary Endpoint in ACTIVATE-KidsT Was Not Met; Results Were Clinically... More