Rocket Pharmaceuticals (RCKT) Highlights Promising Preliminary Results from Phase 1 Trial of Commercial-Grade RP-L102 'Process B' for Fanconi Anemia

Go back to Rocket Pharmaceuticals (RCKT) Highlights Promising Preliminary Results from Phase 1 Trial of Commercial-Grade RP-L102 'Process B' for Fanconi Anemia

Rocket Pharmaceuticals Presents Promising Preliminary Results from Phase 1 Trial of Commercial-Grade RP-L102 “Process B” for Fanconi Anemia at 61st American Society of Hematology Annual Meeting

December 8, 2019 6:00 PM EST

US Phase 1 Trial Establishes Feasibility of Commercial Process B Vector/Cell Manufacturing in FA

Preliminary Data Demonstrate Evidence of Early Engraftment Without Conditioning Four to Six Months after Administration of Gene Therapy

Process B Drug Product VCN 2-3x Higher Than That Administered to Optimally-Treated Process A Patients

NEW YORK--(BUSINESS WIRE)-- Rocket Pharmaceuticals,... More