PTC Therapeutics to present Sephience PKU data at SSIEM 2026

Go back to PTC Therapeutics to present Sephience PKU data at SSIEM 2026

PTC Therapeutics Announces New Sephienceâ„¢ (sepiapterin) Data Reinforcing Broad Patient Benefits Including Sustained Metabolic Control and Diet Liberalization as well as Consistent Favorable Safety P

August 24, 2026 8:00 AM EDT

17 abstracts and presentations planned at SSIEM Symposium

Real-world evidence demonstrates significant diet liberalization achieved with Sephience while maintaining target blood Phe levels

Continued evidence of meaningful benefit across all patient subgroups... More