Alnylam advances Alzheimer's drug trials, reports mivelsiran safety data

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Alnylam Highlights Progress with Neuroscience Programs at AAIC 2026, Showcasing Potential of RNAi in Neurological Disease

July 15, 2026 3:30 AM EDT

Initiates Global Phase 2 APPlauDS Study of Mivelsiran in Down SyndromeAssociated Alzheimers Disease (DS-AD)

Announces Completion of Enrollment in the Phase 2 cAPPricorn-1 Study of Mivelsiran in Cerebral Amyloid Angiopathy (CAA)

Presents Updated Phase 1 Data on Mivelsiran in Early Onset Alzheimers Disease (EOAD) Showing Low Incidence of Amyloid-Related Imaging Abnormalities (ARIA)

Shares Preclinical Data and Design of Ongoing Phase 1 Study of Tau-Targeting ALN5288 in Alzheimers Patients

CAMBRIDGE, Mass.--(BUSINESS... More