Agios receives European approval for PYRUKYND to treat thalassemia

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Agios’ PYRUKYND® (mitapivat) Approved in the European Union for Adults with Thalassemia

May 22, 2026 9:15 AM EDT

PYRUKYND is the only medicine approved in the EU for adults with transfusion-dependent and non-transfusion-dependent alpha- or beta-thalassemia
Mitapivat is now approved for thalassemia in the U.S., Saudi Arabia, United Arab Emirates, and EUAvanzanite Bioscience B.V., a specialty pharmaceutical company, will continue to distribute and commercialize PYRUKYND in Europe

CAMBRIDGE, Mass., May 22, 2026 (GLOBE NEWSWIRE) -- Agios Pharmaceuticals, Inc. (Nasdaq: AGIO), a commercial-stage biopharmaceutical company focused on delivering innovative medicines for patients with rare diseases, today announced that the European Commission (EC) has granted marketing authorization for... More