Precision BioSciences shows muscle improvements in DMD gene therapy study

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Precision BioSciences Presents Preclinical PBGENE-DMD Data Highlighting Durable Dystrophin Expression and Functional Benefit at the Muscular Dystrophy Association Clinical & Scientific Conference

March 10, 2026 7:01 AM EDT

Findings reinforce differentiated in vivo gene editing approach designed for durable functional muscle improvement through satellite cell editing

PBGENE-DMD treatment in a humanized DMD mouse model demonstrates improvements in muscle pathology and biomarkers of muscle damage

PBGENE-DMD shows durable dystrophin protein restoration in humanized DMD mice across key muscle groups, including cardiac, diaphragm, and skeletal muscles

DURHAM, N.C.--(BUSINESS WIRE)-- Precision BioSciences, Inc. (Nasdaq: DTIL), a clinical stage gene editing company utilizing its novel proprietary ARCUS® platform to develop in vivo... More