CRISPR Therapeutics (CRSP) Misses Q4 EPS by 14c; Provides Business Update

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CRISPR Therapeutics (CRSP), Vertex (VRTX) Announce Progress in Clinical Development Programs for Investigational CRISPR/Cas9 Gene-Editing Therapy CTX001

February 25, 2019 8:02 AM EST

CRISPR Therapeutics (NASDAQ: CRSP) and Vertex Pharmaceuticals Incorporated (NASDAQ: VRTX) today reviewed recent progress in the clinical development programs for CTX001, an investigational, autologous, CRISPR/Cas9 gene-edited hematopoietic stem cell therapy being evaluated for patients suffering from severe hemoglobinopathies. The companies announced that the first patient has been treated with CTX001 in a Phase 1/2 clinical study of patients with transfusion-dependent beta thalassemia (TDT), marking the first company-sponsored use of a CRISPR/Cas9 therapy in a clinical trial. In parallel, the companies are investigating CTX001 for the... More