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Alexion Pharma (ALXN) Announces New Long-Term Kanuma Phase 3 Data in LAL-D

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New Long-Term Data Presented at WCPGHAN 2016 Show Rapid and Sustained Improvements in Important Markers of Liver Injury and Lipid Abnormalities in Children and Adults with Lysosomal Acid Lipase Defici

October 6, 2016 4:30 PM EDT

--Achieved Rapid and Sustained Reduction in ALT, a Marker of Liver Injury, in 97 Percent of Kanuma-Treated Patients with LAL-D, including Higher Proportion of Patients Achieving ALT Normalization at 52 Weeks--

NEW HAVEN, Conn.--(BUSINESS WIRE)-- Alexion Pharmaceuticals, Inc. (Nasdaq: ALXN) announced today that researchers presented new long-term data from an ongoing, open-label extension of the pivotal Phase 3 ARISE trial of Kanuma® (sebelipase alfa) in children and adults with lysosomal acid lipase deficiency (LAL-D), a genetic and progressive ultra-rare metabolic disease. At 52 weeks of Kanuma treatment, nearly all patients (97... More