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Retrophin's (RTRX) RE-024 Granted EC Orphan Drug Designation for the Treatment of PKAN

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Retrophin Receives European Orphan Drug Designation for RE-024 for the Treatment of Pantothenate Kinase-Associated Neurodegeneration

February 24, 2016 8:30 AM EST

SAN DIEGO, Feb. 24, 2016 (GLOBE NEWSWIRE) -- Retrophin, Inc. (NASDAQ: RTRX) today announced that the European Commission has granted orphan drug designation to RE-024, the Companys novel investigational phosphopantothenate replacement therapy for pantothenate kinase-associated neurodegeneration (PKAN), a rare and life-threatening genetic disorder with no approved treatment option.  

Receiving orphan drug status in the EU is another encouraging step in the development of RE-024 for the treatment of PKAN, said Alvin Shih, M.D., executive vice president and head of research & development for Retrophin. Without an approved therapy, many people... More