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PTC Therapeutics (PTCT) Commences RG7916 Phase 2 in Type 2/3 SMA Patients with Roche, SMAF

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Spinal Muscular Atrophy Program Advances into Phase 2 Clinical Studies in SMA Patients with RG7916

October 20, 2016 4:30 PM EDT

SOUTH PLAINFIELD, N.J., Oct. 20, 2016 /PRNewswire/ -- PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced that its joint development program in Spinal Muscular Atrophy (SMA) with Roche (SIX: RO, ROG; OTCQX: RHHBY) and the SMA Foundation (SMAF) initiated a Phase 2 study in pediatric and adult Type 2/3 SMA patients. The study, named SUNFISH, is a two-part study investigating the safety, tolerability and efficacy of RG7916, an oral small molecule survival motor neuron 2 (SMN2) splicing modifier. The first part of the study will evaluate safety and tolerability... More