Consistently demonstrated improved vector copy number (VCN) in transfusion-dependent -thalassemia (TDT) and severe sickle cell disease (SCD) patient cells in vitro with manufacturing Process 2
Implementing plan to optimize patient outcomes in severe SCD
Achieved general agreement on regulatory path for TDT across all genotypes, ages
Advanced suspension manufacturing process
NEW YORK--(BUSINESS WIRE)-- bluebird bio, Inc.... More